Ultragenyx reports 96-week gene therapy data showing 61% lower cornstarch use

Verifying
  • Ultragenyx announced publication of 96-week Phase 3 GENGLYCOS data for GSDIa patients.
  • 61% mean cornstarch reduction was achieved by original and crossover participants at Week 96.
  • DTX401 maintained a manageable two-year safety profile without reported class-related toxicity or malignancy.
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